Exploring next steps for patient care

DMD Care UK national meeting held on Rare Disease Day 2024

DRF highlights psychosocial research

Dozens of families attended DUK’s latest parent information day

KineDMD published in Nature Medicine

Ground-breaking DRF-funded study published and featured on BBC

Parents urged to read new cardiac recommendations

DMD Care UK guidance published in BMJ Open Heart journal

Dedicated mental health support put in place for Duchenne families

DRF-funded programme has appointed two psychiatrists and a psychologist to tackle lack of support

DRF-funded post made permanent

Vital physiotherapist post made permanent by GOSH Trust

Solid acquires AavantiBio

Merger completed, as Solid focuses on next generation gene therapy

£6m raised for Duchenne research

Cutting edge research in clinical trial thanks to your generosity.

Watch now: An Evening with DRF

Catch up on Gavriel Rosenfeld in conversation with Dr Ronni Cohn

DRF-funded drug shows success in clinical trial

Vamorolone, an alternative to steroids, has shown positive results in Phase 2 trial.

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy: 
the biggest genetic killer of children worldwide

Exploring next steps for patient care

DMD Care UK national meeting held on Rare Disease Day 2024

DRF highlights psychosocial research

Dozens of families attended DUK’s latest parent information day

KineDMD published in Nature Medicine

Ground-breaking DRF-funded study published and featured on BBC

Parents urged to read new cardiac recommendations

DMD Care UK guidance published in BMJ Open Heart journal

Dedicated mental health support put in place for Duchenne families

DRF-funded programme has appointed two psychiatrists and a psychologist to tackle lack of support

DRF-funded post made permanent

Vital physiotherapist post made permanent by GOSH Trust

Solid acquires AavantiBio

Merger completed, as Solid focuses on next generation gene therapy

£6m raised for Duchenne research

Cutting edge research is in clinical trial thanks to your generosity.

Watch now: An Evening with DRF

Catch up on Gavriel Rosenfeld in conversation with Dr Ronni Cohn

DRF-funded drug shows success in clinical trial

Vamorolone, an alternative to steroids, shows positive results in Phase 2 trial

Finding a cure for Duchenne

We accelerate treatments for Duchenne muscular dystrophy:
the biggest genetic killer of children worldwide

MILLION pounds raised thanks to our dedicated supporters

projects funded to help combat the biggest genetic killer of children

other patient organisations with which we have proudly collaborated

Our mission

We aim to stop Duchenne muscular dystrophy being a death sentence for hundreds of thousands of boys worldwide.

Our impact

We are helping turn the hope of treatments into reality. Critical treatments are in clinical trial thanks to our funds.

Your help

Your generosity has funded millions of pounds worth of  ground-breaking research. And there is still work to do.